Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

A new Israeli-led study identifies an RNA-based therapy that may halt ALS progression and regenerate nerve cells.

In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn ...

Genetic errors can cause many different diseases, and scientists have been looking for methods to fix those errors for decades. Although many gene therapies have aimed to correct errors in individual ...

We have written about the promise of gene therapy to correct genetic disease many times. An exciting development happened ...

Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them closer to genetic switches on the DNA called enhancers. The intermediate ...

As per SNS Insider Research, The DNA Manufacturing Market growth is driven by plasmid DNA demand, biopharma innovation, and advancements in DNA-based vaccine production.Austin, Nov. 07, 2025 (GLOBE ...

MavriX Bio, a clinical-stage biotechnology company focused on the development of transformative genetic therapies for Angelman syndrome (AS), today announced that the first patient has been dosed in ...