Penn and CHOP researchers want to develop urea cycle disorder treatments using CRISPR gene-editing therapy. Get unlimited access to Inquirer.com and The Inquirer App, plus 5 articles each month to ...
Promising results from a small clinical trial highlight a growing interest in designing gene-editing treatments for common ...
A sponsor will have to demonstrate success with "with several consecutive patients with different bespoke therapies" to ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback